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Logo of jcinvestThe Journal of Clinical Investigation
J Clin Invest. 1990 May; 85(5): 1343–1352.
PMCID: PMC296579

Alpha 1-antitrypsin deficiency, emphysema, and liver disease. Genetic basis and strategies for therapy.

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Selected References

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  • Garver RI, Jr, Chytil A, Courtney M, Crystal RG. Clonal gene therapy: transplanted mouse fibroblast clones express human alpha 1-antitrypsin gene in vivo. Science. 1987 Aug 14;237(4816):762–764. [PubMed]
  • Grossman A, Silver RT, Arlin Z, Coleman M, Camposano E, Gascon P, Benn PA. Fine mapping of chromosome 22 breakpoints within the breakpoint cluster region (bcr) implies a role for bcr exon 3 in determining disease duration in chronic myeloid leukemia. Am J Hum Genet. 1989 Nov;45(5):729–738. [PubMed]

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